Viewing StudyNCT02999984



Ignite Creation Date: 2024-05-06 @ 9:30 AM
Last Modification Date: 2024-10-26 @ 12:15 PM
Study NCT ID: NCT02999984
Status: COMPLETED
Last Update Posted: 2022-08-03
First Post: 2016-12-19

Brief Title: Efficacy and Safety of the Cryopreserved Formulation of OTL-101 in Subjects With ADA-SCID
Sponsor: University of California Los Angeles
Organization: University of California Los Angeles

Organization Data

Organization: University of California Los Angeles
Class: OTHER
Study ID: OTL-101-4
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor: University of California Los Angeles
Lead Sponsor Class: OTHER
Responsible Party: Donald B Kohn MD
Responsible Party Title: Principal Investigator
Responsible Party Type: PRINCIPAL_INVESTIGATOR
Responsible Party Affiliation: University of California Los Angeles
Old Name: None
Old Organization: None

Collaborators

Name Class
Orchard Therapeutics INDUSTRY
California Institute for Regenerative Medicine CIRM OTHER