Viewing Study NCT07399704


Ignite Creation Date: 2026-03-26 @ 3:16 PM
Ignite Modification Date: 2026-03-30 @ 1:16 AM
Study NCT ID: NCT07399704
Status: RECRUITING
Last Update Posted: 2026-03-19
First Post: 2025-12-17
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: A Study to Evaluate the Safety and Efficacy of Nizubaglustat (AZ-3102) in Patients With GM2 Gangliosidosis or Niemann-Pick Type C Disease
Sponsor: Azafaros A.G.
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: AZA-001-5A2-02
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators