Viewing Study NCT05567627


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Study NCT ID: NCT05567627
Status: UNKNOWN
Last Update Posted: 2023-11-01
First Post: 2022-09-25
Is Possible Gene Therapy: True
Is NOT Gene Therapy: False
Has Adverse Events: False

Brief Title: Clinical Exploration of Adeno-associated Virus (AAV) Expressing Human Acid Alpha- Glucosidase (GAA) Gene Therapy for Patients With Infantile-onset Pompe Disease
Sponsor: Seventh Medical Center of PLA General Hospital
Organization:

Organization Data

Organization:
Class: OTHER
Study ID: JLJY-GC301-IOPD-003
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: OTHER
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators

Collaborators

Name Class View
None UNKNOWN View