Viewing StudyNCT01852071



Ignite Creation Date: 2024-05-06 @ 1:37 AM
Last Modification Date: 2024-10-26 @ 11:06 AM
Study NCT ID: NCT01852071
Status: COMPLETED
Last Update Posted: 2022-08-03
First Post: 2013-05-07

Brief Title: Autologous CD34 Hematopoietic Stem Cells Transduced ex Vivo With Elongation Factor 1 Alpha Shortened EFS Lentiviral Vector Encoding for the Human ADA Gene
Sponsor: University of California Los Angeles
Organization: University of California Los Angeles

Organization Data

Organization: University of California Los Angeles
Class: OTHER
Study ID: EFS-ADA
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor: University of California Los Angeles
Lead Sponsor Class: OTHER
Responsible Party: Donald B Kohn MD
Responsible Party Title: Principal Investigator
Responsible Party Type: PRINCIPAL_INVESTIGATOR
Responsible Party Affiliation: University of California Los Angeles
Old Name: None
Old Organization: None

Collaborators

Name Class
Orchard Therapeutics INDUSTRY
National Institute of Allergy and Infectious Diseases NIAID NIH
National Human Genome Research Institute NHGRI NIH
National Heart Lung and Blood Institute NHLBI NIH