Viewing Study NCT06856759


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Ignite Modification Date: 2026-01-31 @ 9:15 PM
Study NCT ID: NCT06856759
Status: RECRUITING
Last Update Posted: 2025-07-01
First Post: 2024-12-29
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Single-Dose AAV-MECP2 Safety/Tolerability and Efficacy in Rett Syndrome
Sponsor: Guangzhou Women and Children's Medical Center
Organization:

Organization Data

Organization:
Class: OTHER
Study ID: 2024-433A01
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: OTHER
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators