Viewing Study NCT03779334


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Study NCT ID: NCT03779334
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-11-26
First Post: 2018-12-17
Is NOT Gene Therapy: True
Has Adverse Events: True

Brief Title: A Study of Risdiplam in Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy
Sponsor: Hoffmann-La Roche
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: BN40703
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators