Viewing Study NCT04925960


Ignite Creation Date: 2025-12-25 @ 2:10 AM
Ignite Modification Date: 2026-01-06 @ 6:21 PM
Study NCT ID: NCT04925960
Status: TERMINATED
Last Update Posted: 2025-09-25
First Post: 2021-06-08
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Oral Epalrestat Therapy in Pediatric Subjects With PMM2-CDG
Sponsor: Maggie's Pearl, LLC
Organization:

Organization Data

Organization:
Class: INDUSTRY
Study ID: 21-000492
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor:
Lead Sponsor Class: INDUSTRY
Responsible Party:
Responsible Party Title:
Responsible Party Type: SPONSOR
Responsible Party Affiliation:
Old Name: None
Old Organization: None

Collaborators