Viewing Study NCT02193867


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Study NCT ID: NCT02193867
Status: TERMINATED
Last Update Posted: 2019-11-18
First Post: 2014-07-07
Is Gene Therapy: True
Has Adverse Events: True

Brief Title: Clinical Study In Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency
Sponsor: Alexion Pharmaceuticals, Inc.
Organization: