Viewing Study NCT04601051

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Ignite Creation Date: 2025-12-24 @ 11:55 PM

Ignite Modification Date: 2025-12-25 @ 9:51 PM

Study NCT ID: NCT04601051

Status: ACTIVE_NOT_RECRUITING

Last Update Posted: 2025-05-01

First Post: 2020-10-19

Is NOT Gene Therapy: False

Has Adverse Events: False

Brief Title: Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of NTLA-2001 in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy (ATTRv-PN) and Patients With Transthyretin Amyloidosis-Related Cardiomyopathy (ATTR-CM)

Sponsor: Intellia Therapeutics

Organization:

Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module