Viewing Study NCT06283212


Ignite Creation Date: 2025-12-26 @ 10:44 PM
Ignite Modification Date: 2025-12-26 @ 10:44 PM
Study NCT ID: NCT06283212
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-12-12
First Post: 2024-02-22
Is Possible Gene Therapy: True
Is NOT Gene Therapy: False
Has Adverse Events: False

Brief Title: A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Children With SCN1A-positive Dravet Syndrome
Sponsor: Encoded Therapeutics
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module