Viewing Study NCT06615206


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Study NCT ID: NCT06615206
Status: RECRUITING
Last Update Posted: 2024-11-26
First Post: 2024-09-04
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: A First-in-Human Clinical Trial to Evaluate the Safety, Tolerability, and Efficacy of a Novel CRISPR RNA-editing Therapy in Patients with Mecp2 Duplication Syndrome, a Rare Orphan Disease (HERO)
Sponsor: HuidaGene Therapeutics Co., Ltd.
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module