Viewing Study NCT04516369


Ignite Creation Date: 2025-12-24 @ 11:09 PM
Ignite Modification Date: 2025-12-25 @ 8:43 PM
Study NCT ID: NCT04516369
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-04-25
First Post: 2020-08-10
Is NOT Gene Therapy: False
Has Adverse Events: False

Brief Title: Study of Efficacy and Safety of Voretigene Neparvovec in Japanese Patients With Biallelic RPE65 Mutation-associated Retinal Dystrophy
Sponsor: Novartis Pharmaceuticals
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module