Ignite Creation Date:
2025-12-24 @ 11:00 PM
Ignite Modification Date:
2026-01-01 @ 2:42 PM
Study NCT ID:
NCT05001269
Status:
COMPLETED
Last Update Posted:
2025-10-30
First Post:
2021-06-30
Is NOT Gene Therapy:
True
Has Adverse Events:
False
Brief Title:
Nedosiran in Pediatric Patients From Birth to 11 Years of Age With PH and Relatively Intact Renal Function
Sponsor:
Dicerna Pharmaceuticals, Inc., a Novo Nordisk company