Ignite Creation Date:
2025-12-24 @ 10:41 PM
Ignite Modification Date:
2025-12-28 @ 8:35 AM
Study NCT ID:
NCT04669535
Status:
TERMINATED
Last Update Posted:
2025-09-02
First Post:
2020-11-23
Is Gene Therapy:
True
Has Adverse Events:
True
Brief Title:
A Dose-escalation and Safety & Efficacy Study of AXO-AAV-GM2 in Tay-Sachs or Sandhoff Disease
Sponsor:
Terence Flotte
Organization:
Study Modules
Identification Module
Status Module
Sponsor Collaborators Module
Oversight Module
Description Module
Conditions Module
Design Module
Arms Interventions Module
Outcomes Module
Eligibility Module
Contacts Locations Module
References Module
Adverse Events Module
Baseline Characteristics Module
Participant Flow Module