Viewing Study NCT06178432


Ignite Creation Date: 2025-12-24 @ 9:24 PM
Ignite Modification Date: 2026-02-11 @ 2:37 AM
Study NCT ID: NCT06178432
Status: NOT_YET_RECRUITING
Last Update Posted: 2023-12-21
First Post: 2023-11-30
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Evaluation of the Safety, Tolerability and Efficacy of Gene Therapy Drug for Late Onset Pompe Disease (LOPD)
Sponsor: Huashan Hospital
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module