Viewing Study NCT03311503


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Ignite Modification Date: 2026-02-25 @ 10:05 PM
Study NCT ID: NCT03311503
Status: RECRUITING
Last Update Posted: 2025-12-11
First Post: 2017-10-12
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Phase I/II Trial of Lentiviral Gene Transfer for SCID-X1 With Low Dose Targeted Busulfan Conditioning
Sponsor: David Williams
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module