Viewing Study NCT06904261


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Ignite Modification Date: 2025-12-27 @ 10:10 PM
Study NCT ID: NCT06904261
Status: RECRUITING
Last Update Posted: 2025-12-04
First Post: 2025-03-13
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants
Sponsor: Amicus Therapeutics
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module