Viewing Study NCT01634750


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Study NCT ID: NCT01634750
Status: COMPLETED
Last Update Posted: 2017-10-19
First Post: 2012-07-03
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Phase I Clinical Trial of ManNAc in Patients With GNE Myopathy or Hereditary Inclusion Body Myopathy (HIBM)
Sponsor: National Human Genome Research Institute (NHGRI)
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module