Viewing Study NCT04721366


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Ignite Modification Date: 2026-01-01 @ 8:27 PM
Study NCT ID: NCT04721366
Status: COMPLETED
Last Update Posted: 2024-03-29
First Post: 2021-01-21
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: A Study of Velaglucerase Alfa (VPRIV) Given as Standard Patient Care in Young Children With Gaucher Disease
Sponsor: Takeda
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module