Viewing Study NCT05665166


Ignite Creation Date: 2025-12-24 @ 4:15 PM
Ignite Modification Date: 2025-12-28 @ 7:24 PM
Study NCT ID: NCT05665166
Status: RECRUITING
Last Update Posted: 2024-10-02
First Post: 2022-12-07
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Gene Therapy with Modified Autologous Hematopoietic Stem Cells for Patients with Mucopolysaccharidosis Type II
Sponsor: University of Manchester
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module