Viewing Study NCT03652259


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Study NCT ID: NCT03652259
Status: TERMINATED
Last Update Posted: 2025-09-10
First Post: 2018-08-28
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Gene Delivery Clinical Trial of SRP-9003 (Bidridistrogene Xeboparvovec) for Participants With Limb-Girdle Muscular Dystrophy, Type 2E (LGMD2E) (Beta-Sarcoglycan Deficiency)
Sponsor: Sarepta Therapeutics, Inc.
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module