Viewing Study NCT03548220


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Study NCT ID: NCT03548220
Status: COMPLETED
Last Update Posted: 2022-05-24
First Post: 2018-05-24
Is NOT Gene Therapy: False
Has Adverse Events: True

Brief Title: A Study to Evaluate Efficacy and Safety of AG-348 in Not Regularly Transfused Adult Participants With Pyruvate Kinase Deficiency (PKD)
Sponsor: Agios Pharmaceuticals, Inc.
Organization: