Viewing Study NCT04041102


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Study NCT ID: NCT04041102
Status: COMPLETED
Last Update Posted: 2025-10-24
First Post: 2019-07-16
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Natural History Study of Infantile and Juvenile GM1 Gangliosidosis (GM1) Patients
Sponsor: University of Pennsylvania
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module