Viewing Study NCT04041102


Ignite Creation Date: 2025-12-25 @ 3:39 AM
Ignite Modification Date: 2025-12-26 @ 2:24 AM
Study NCT ID: NCT04041102
Status: COMPLETED
Last Update Posted: 2025-10-24
First Post: 2019-07-16
Is NOT Gene Therapy: False
Has Adverse Events: False

Brief Title: Natural History Study of Infantile and Juvenile GM1 Gangliosidosis (GM1) Patients
Sponsor: University of Pennsylvania
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module