Viewing Study NCT05951205


Ignite Creation Date: 2025-12-25 @ 3:30 AM
Ignite Modification Date: 2025-12-26 @ 2:11 AM
Study NCT ID: NCT05951205
Status: NOT_YET_RECRUITING
Last Update Posted: 2025-07-02
First Post: 2023-06-23
Is NOT Gene Therapy: False
Has Adverse Events: False

Brief Title: Evaluation of Efficacy and Safety of a Single Dose of Exa-cel in Participants With Severe Sickle Cell Disease, βS/βC Genotype
Sponsor: Vertex Pharmaceuticals Incorporated
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module