Viewing Study NCT04069533


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Study NCT ID: NCT04069533
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2024-05-22
First Post: 2019-08-23
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype A
Sponsor: Rocket Pharmaceuticals Inc.
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module