Ignite Creation Date:
2025-12-25 @ 2:46 AM
Ignite Modification Date:
2025-12-26 @ 1:27 AM
Study NCT ID:
NCT03887533
Status:
TERMINATED
Last Update Posted:
2022-08-30
First Post:
2019-03-22
Is NOT Gene Therapy:
False
Has Adverse Events:
True
Brief Title:
Combined Intrathecal and Intravenous VTS-270 Therapy for Liver and Neurological Disease Associated With Niemann-Pick Disease, Type C1
Sponsor:
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)