Viewing Study NCT05073133

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Ignite Creation Date: 2025-12-25 @ 2:42 AM

Ignite Modification Date: 2025-12-30 @ 10:00 PM

Study NCT ID: NCT05073133

Status: COMPLETED

Last Update Posted: 2024-10-09

First Post: 2021-09-20

Is Gene Therapy: True

Has Adverse Events: True

Brief Title: Safety and Efficacy of Intravenous OAV101 (AVXS-101) in Pediatric Patients With Spinal Muscular Atrophy (SMA) (OFELIA)

Sponsor: Novartis Pharmaceuticals

Organization:

Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module Adverse Events Module Baseline Characteristics Module Participant Flow Module