Viewing Study NCT04049760

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Ignite Modification Date: 2025-12-27 @ 11:51 PM

Study NCT ID: NCT04049760

Status: COMPLETED

Last Update Posted: 2025-06-17

First Post: 2019-07-30

Is NOT Gene Therapy: True

Has Adverse Events: True

Brief Title: Safety, Pharmacodynamics, and Efficacy of Migalastat in Pediatric Subjects (Aged >12 Years) With Fabry Disease

Sponsor: Amicus Therapeutics

Organization:

Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module Adverse Events Module Baseline Characteristics Module Participant Flow Module