Viewing Study NCT04925960


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Ignite Modification Date: 2025-12-27 @ 10:40 AM
Study NCT ID: NCT04925960
Status: TERMINATED
Last Update Posted: 2025-09-25
First Post: 2021-06-08
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Oral Epalrestat Therapy in Pediatric Subjects With PMM2-CDG
Sponsor: Maggie's Pearl, LLC
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module