Viewing Study NCT01009294


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Study NCT ID: NCT01009294
Status: TERMINATED
Last Update Posted: 2020-07-29
First Post: 2009-11-05
Is NOT Gene Therapy: True
Has Adverse Events: True

Brief Title: Study of Ataluren (PTC124) in Nonambulatory Participants With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD)
Sponsor: PTC Therapeutics
Organization: