Viewing Study NCT02112994


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Study NCT ID: NCT02112994
Status: COMPLETED
Last Update Posted: 2019-12-04
First Post: 2014-03-20
Is NOT Gene Therapy: True
Has Adverse Events: True

Brief Title: Safety and Efficacy Study of Sebelipase Alfa in Participants With Lysosomal Acid Lipase Deficiency
Sponsor: Alexion Pharmaceuticals, Inc.
Organization: