Viewing Study NCT03488394

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Ignite Creation Date: 2025-12-25 @ 1:34 AM

Ignite Modification Date: 2025-12-25 @ 11:48 PM

Study NCT ID: NCT03488394

Status: ACTIVE_NOT_RECRUITING

Last Update Posted: 2025-12-09

First Post: 2018-03-22

Is Possible Gene Therapy: True

Is NOT Gene Therapy: True

Has Adverse Events: False

Brief Title: Gene Therapy With Modified Autologous Hematopoietic Stem Cells for the Treatment of Patients With Mucopolysaccharidosis Type I, Hurler Variant

Sponsor: Orchard Therapeutics

Organization:

Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module