Ignite Creation Date:
2025-12-24 @ 11:32 PM
Ignite Modification Date:
2026-02-25 @ 2:36 AM
Study NCT ID:
NCT01839656
Status:
COMPLETED
Last Update Posted:
2021-02-17
First Post:
2013-04-22
Is NOT Gene Therapy:
True
Has Adverse Events:
True
Brief Title:
A Study to Assess the Efficacy, Safety and Pharmacokinetics of Nusinersen (ISIS 396443) in Infants With Spinal Muscular Atrophy (SMA)
Sponsor:
Organization: