Viewing Study NCT01275066


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Study NCT ID: NCT01275066
Status: COMPLETED
Last Update Posted: 2014-07-07
First Post: 2011-01-10
Is Gene Therapy: True
Has Adverse Events: True

Brief Title: A Double-Blind Study to Evaluate the Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)
Sponsor:
Organization: