Ignite Creation Date:
2025-12-24 @ 4:37 PM
Ignite Modification Date:
2026-01-26 @ 10:51 PM
Study NCT ID:
NCT02230566
Status:
COMPLETED
Last Update Posted:
2020-07-30
First Post:
2014-08-22
Is Gene Therapy:
True
Has Adverse Events:
True
Brief Title:
A Phase 3 Study of UX003 Recombinant Human Betaglucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With Mucopolysaccharidosis Type 7 (MPS 7)
Sponsor:
Organization: