Viewing StudyNCT03461289



Ignite Creation Date: 2024-05-06 @ 11:13 AM
Last Modification Date: 2024-10-26 @ 12:42 PM
Study NCT ID: NCT03461289
Status: COMPLETED
Last Update Posted: 2022-08-16
First Post: 2018-03-04

Brief Title: Single-Dose Gene Replacement Therapy Clinical Trial for Participants With Spinal Muscular Atrophy Type 1
Sponsor:
Organization: Novartis