Ignite Creation Date:
2024-05-06 @ 3:47 PM
Last Modification Date:
2024-10-26 @ 1:57 PM
Study NCT ID:
NCT04755751
Status:
UNKNOWN
Last Update Posted:
2021-02-16
First Post:
2021-02-10
Brief Title:
Exercise Capacity in Response to Enzyme Replacement Therapy in Pediatric Pompe Disease
Sponsor:
Organization:
Rambam Health Care Campus
Study Design
Study Type:
OBSERVATIONAL
Expanded Access Type Individual:
None
Expanded Access Type Intermediate:
None
Expanded Access Type Treatment:
None
Patient Registry:
False
Target Duration:
None
Design Allocation:
Design Intervention Model:
Design Intervention Model Description:
Design Masking Description:
Bio Spec Retention:
SAMPLES_WITHOUT_DNA
Bio Spec Description:
self-collected blood samples on a Guthrie card for enzyme blood levels
Enrollment Count:
4
Enrollment Type:
ESTIMATED
Design Primary Purpose:
Design Masking:
Phases:
Observational Models:
| Name |
|---|
| Case-Only |
Time Perspective List:
Clinical Trial Statuses
| Name |
|---|
| 72695 |
Who Masked List: