Ignite Creation Date:
2024-05-06 @ 2:18 PM
Last Modification Date:
2024-10-26 @ 1:28 PM
Study NCT ID:
NCT04273243
Status:
ACTIVE_NOT_RECRUITING
Last Update Posted:
2023-02-06
First Post:
2020-02-14
Brief Title:
Long-Term Follow Up of CLN6 Batten Disease Subjects Following Gene Transfer
Sponsor:
Organization:
Amicus Therapeutics
Study Design
Study Type:
OBSERVATIONAL
Expanded Access Type Individual:
None
Expanded Access Type Intermediate:
None
Expanded Access Type Treatment:
None
Patient Registry:
False
Target Duration:
None
Design Allocation:
Design Intervention Model:
Design Intervention Model Description:
Design Masking Description:
Bio Spec Retention:
SAMPLES_WITH_DNA
Bio Spec Description:
During the study blood samples will be taken for routine lab tests and future tests for safety effectiveness or other research assessments
Enrollment Count:
10
Enrollment Type:
ACTUAL
Design Primary Purpose:
Design Masking:
Phases:
Observational Models:
| Name |
|---|
| Case-Only |
Time Perspective List:
Clinical Trial Statuses
| Name |
|---|
| 62399 |
Who Masked List: