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Ignite Creation Date: 2024-05-06 @ 3:17 PM
Last Modification Date: 2024-10-26 @ 1:46 PM
Study NCT ID: NCT04581785
Status: TERMINATED
Last Update Posted: 2024-02-23
First Post: 2020-10-02

Brief Title: Gene Therapy With hLB-001 in Pediatric Patients With Severe Methylmalonic Acidemia
Sponsor:
Organization: Alexion Pharmaceuticals Inc