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Ignite Creation Date: 2024-05-06 @ 12:30 PM
Last Modification Date: 2024-10-26 @ 12:59 PM
Study NCT ID: NCT03770572
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2023-08-29
First Post: 2018-12-07

Brief Title: Gene Therapy for Children With CLN3 Batten Disease
Sponsor:
Organization: Amicus Therapeutics