Viewing Study NCT06178393


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Ignite Modification Date: 2025-12-25 @ 11:18 PM
Study NCT ID: NCT06178393
Status: COMPLETED
Last Update Posted: 2023-12-21
First Post: 2023-12-11
Is NOT Gene Therapy: False
Has Adverse Events: False

Brief Title: Real-World Use of Novel Treatments in Patients With Spinal Muscular Atrophy (SMA): A Multi-Site Retrospective Chart Review of Pediatric SMA Patients Outside of the United States
Sponsor: Novartis Pharmaceuticals
Organization:

Key Dates - Follows AllAPIJSON File Order

Start Date: 2022-05-05
Start Date Type: ACTUAL
Primary Completion Date: 2022-12-30
Primary Completion Date Type: ACTUAL
Completion Date: 2022-12-30
Completion Date Type: ACTUAL
First Submit Date: 2023-12-11
First Submit QC Date: None
Study First Post Date: 2023-12-21
Study First Post Date Type: ACTUAL
Results First Submit Date: None
Results First Submit QC Date: None
Results First Post Date: None
Results First Post Date Type: None
Results First Post QC Date: None
Results First Post QC Date Type: None
Disp First Submit Date: None
Disp First Submit QC Date: None
Disp First Post Date: None
Disp First Post Date Type: None
Last Update Submit Date: 2023-12-11
Last Update Post Date: 2023-12-21
Last Update Post Date Type: ACTUAL