Ignite Creation Date:
2025-12-24 @ 10:41 PM
Ignite Modification Date:
2025-12-28 @ 8:35 AM
Study NCT ID:
NCT04669535
Status:
TERMINATED
Last Update Posted:
2025-09-02
First Post:
2020-11-23
Is Gene Therapy:
True
Has Adverse Events:
True
Brief Title:
A Dose-escalation and Safety & Efficacy Study of AXO-AAV-GM2 in Tay-Sachs or Sandhoff Disease
Sponsor:
Terence Flotte
Organization:
Key Dates - Follows AllAPIJSON File Order
Start Date:
2021-01-15
Start Date Type:
ACTUAL
Primary Completion Date:
2024-05-23
Primary Completion Date Type:
ACTUAL
Completion Date:
2024-12-16
Completion Date Type:
ACTUAL
First Submit Date:
2020-11-23
First Submit QC Date:
None
Study First Post Date:
2020-12-17
Study First Post Date Type:
ACTUAL
Results First Submit Date:
2025-04-04
Results First Submit QC Date:
None
Results First Post Date:
2025-05-22
Results First Post Date Type:
ACTUAL
Results First Post QC Date:
None
Results First Post QC Date Type:
None
Disp First Submit Date:
None
Disp First Submit QC Date:
None
Disp First Post Date:
None
Disp First Post Date Type:
None
Last Update Submit Date:
2025-08-12
Last Update Post Date:
2025-09-02
Last Update Post Date Type:
ESTIMATED