Viewing Study NCT05567627


Ignite Creation Date: 2025-12-25 @ 5:19 AM
Ignite Modification Date: 2025-12-26 @ 4:26 AM
Study NCT ID: NCT05567627
Status: UNKNOWN
Last Update Posted: 2023-11-01
First Post: 2022-09-25
Is Possible Gene Therapy: True
Is NOT Gene Therapy: False
Has Adverse Events: False

Brief Title: Clinical Exploration of Adeno-associated Virus (AAV) Expressing Human Acid Alpha- Glucosidase (GAA) Gene Therapy for Patients With Infantile-onset Pompe Disease
Sponsor: Seventh Medical Center of PLA General Hospital
Organization:

Key Dates - Follows AllAPIJSON File Order

Start Date: 2022-08-01
Start Date Type: ACTUAL
Primary Completion Date: 2024-09
Primary Completion Date Type: ESTIMATED
Completion Date: 2025-09
Completion Date Type: ESTIMATED
First Submit Date: 2022-09-25
First Submit QC Date: None
Study First Post Date: 2022-10-05
Study First Post Date Type: ACTUAL
Results First Submit Date: None
Results First Submit QC Date: None
Results First Post Date: None
Results First Post Date Type: None
Results First Post QC Date: None
Results First Post QC Date Type: None
Disp First Submit Date: None
Disp First Submit QC Date: None
Disp First Post Date: None
Disp First Post Date Type: None
Last Update Submit Date: 2023-10-30
Last Update Post Date: 2023-11-01
Last Update Post Date Type: ACTUAL