Ignite Creation Date:
2025-12-25 @ 2:10 AM
Ignite Modification Date:
2025-12-27 @ 10:40 AM
Study NCT ID:
NCT04925960
Status:
TERMINATED
Last Update Posted:
2025-09-25
First Post:
2021-06-08
Is NOT Gene Therapy:
True
Has Adverse Events:
False
Brief Title:
Oral Epalrestat Therapy in Pediatric Subjects With PMM2-CDG
Sponsor:
Maggie's Pearl, LLC