Viewing StudyNCT01242111



Ignite Creation Date: 2024-05-05 @ 11:03 PM
Last Modification Date: 2024-10-26 @ 10:27 AM
Study NCT ID: NCT01242111
Status: TERMINATED
Last Update Posted: 2015-09-30
First Post: 2010-10-28

Brief Title: A Study to Evaluate the Long-Term Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA Morquio A Syndrome
Sponsor: BioMarin Pharmaceutical
Organization: BioMarin Pharmaceutical

Conditions & Keywords Data

Conditions:
Name
MPS IV A
Mucopolysaccharidosis IVA
Morquio A Syndrome
Keywords:
Name View
ERT View
Mucopolysaccharidosis IV type A View
MPS IV Type A View
Mucopolysaccharidosis IVA View
MPS IVA View
Morquio A Syndrome View
Lysosomal Storage Disorder View
LSD View
N-acetylgalactosamine-6-sulfatase View
N-acetylgalactosamine-6-sulfate sulfatase View
galactose-6-sulfatase View
GALNS View
enzyme replacement therapy View