Viewing Study NCT02629393


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Study NCT ID: NCT02629393
Status: COMPLETED
Last Update Posted: 2023-10-17
First Post: 2015-12-03
Is Gene Therapy: True
Has Adverse Events: True

Brief Title: Study of ORGN001 (Formerly ALXN1101) in Neonates, Infants and Children With Molybdenum Cofactor Deficiency (MOCD) Type A
Sponsor: Origin Biosciences
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Molybdenum Cofactor Deficiency, Type A View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Molybdenum Cofactor Deficiency (MoCD) View
None Molybdenum Cofactor (MoCo) biosynthesis View
None sulfite oxidase (SO) View
None S sulfocysteine (SSC) View
None xanthine oxidoreductase View
None aldehyde oxidase View