Viewing Study NCT01416467


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Study NCT ID: NCT01416467
Status: COMPLETED
Last Update Posted: 2018-10-11
First Post: 2011-08-11
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Characterization of the Patient Population With Galactosialidosis
Sponsor: St. Jude Children's Research Hospital
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Galactosialidosis View
Keywords:

Keywords

Keyword Brief Keyword Text View
None lysosomal storage disease View
None AAV vector View
None gene transfer View
None disease characterization View