Viewing Study NCT06503367


Ignite Creation Date: 2025-12-25 @ 12:43 AM
Ignite Modification Date: 2026-02-25 @ 11:04 PM
Study NCT ID: NCT06503367
Status: RECRUITING
Last Update Posted: 2025-08-12
First Post: 2024-06-21
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Observation Study in Patients Age 0-5 Years With LAMA2-related Congenital Muscular Dystrophy
Sponsor: Nationwide Children's Hospital
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None LAMA2-MD \(Merosin Deficient Congenital Muscular Dystrophy, MDC1A\) View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Early Phase 1 View
None Observational View
None Natural History View
None Neuromuscular View
None Functional Assessments View