Viewing Study NCT06934967


Ignite Creation Date: 2025-12-25 @ 12:39 AM
Ignite Modification Date: 2026-02-24 @ 3:17 PM
Study NCT ID: NCT06934967
Status: RECRUITING
Last Update Posted: 2025-12-23
First Post: 2025-03-31
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Study to Assess the Pharmacokinetics, Safety, and Tolerability of Iptacopan in Pediatric PNH Patients
Sponsor: Novartis Pharmaceuticals
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Paroxysmal Nocturnal Hemoglobinuria (PNH) View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Iptacopan, View
None PNH, View
None hemoglobin, View
None anemia View