Viewing Study NCT02576795


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Study NCT ID: NCT02576795
Status: COMPLETED
Last Update Posted: 2025-04-10
First Post: 2015-10-05
Is NOT Gene Therapy: True
Has Adverse Events: True

Brief Title: Gene Therapy Study in Severe Haemophilia A Patients (270-201)
Sponsor: BioMarin Pharmaceutical
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Severe Haemophilia A View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Haemophilia A View
None Gene Therapy View
None Clotting Disorders View
None Blood Disorder View
None Blood Coagulation Disorders, Inherited View
None Blood Coagulation Disorders View
None Hematologic Diseases View
None Coagulation Protein Disorders View
None Hemorrhagic Disorders View
None Genetic Diseases, Inborn View
None Factor VIII View
None Coagulants View
None AAV5 vector View